Guanidinylated Neomycin Conjugation Enhances Intranasal Enzyme Replacement in the Brain
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چکیده
منابع مشابه
Adjunctive albuterol enhances the response to enzyme replacement therapy in late-onset Pompe disease.
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ژورنال
عنوان ژورنال: Molecular Therapy
سال: 2017
ISSN: 1525-0016
DOI: 10.1016/j.ymthe.2017.08.007